| Englischer Name | Forschungscode | Forschungsphase | Firma | Indikationen | Klinische Studie |
|---|---|---|---|---|---|
| Tarperprumig | ALXN-1820 | Phase 2 Clinical | Alexion Pharmaceuticals Inc | Anemia, Sickle Cell | Details |
| NM-5072 | NM5072; NM-5072 | Phase 1 Clinical | NovelMed Therapeutics Inc | Hemoglobinuria, Paroxysmal | Details |